1. Executive Summary
2. Research Methodology
3. Spinal Muscular Atrophy
3.1 Overview
3.1.1 Types of Diseases
3.1.2 Symptoms of SMA
3.1.3 Diagnosis of SMA
3.2 Therapy for SMA
4. Market Analysis
4.1 Market Sizing (Actual & Forecasted)
4.1.1 Market Sizing by Value (Actual & Forecasted)
4.1.2 Market Sizing by Volume (Actual & Forecasted)
4.2 Market Share Analysis
4.2.1 Market Share by Disease Type
4.2.2 Market Share by Route of Administration
4.2.3 Market Share by Region
4.2.4 Market Share by Patient Age-Group
5. Market Segmentation by Drugs
5.1 Spinraza
5.1.1 Overview
5.1.2 Market Sizing (Actual & Forecasted)
5.2 Branaplam
5.2.1 Overview
5.3 Reldesemtiv
5.3.1 Overview
5.3.2 Market Sizing (Actual & Forecasted)
6. Regional Analysis
6.1 North America - The US
6.1.1 Market Sizing by Value (Actual & Forecasted)
6.1.2 Market Sizing by Volume (Actual & Forecasted)
6.1.3 Market Share by Treatment
6.1.4 Market Share by Prevalence of Disease
6.2 Europe
6.2.1 Market Sizing by Value (Actual & Forecasted)
6.2.2 Market Sizing by Volume (Actual & Forecasted)
7. Market Dynamics
7.1 Industry Trends & Developments
7.1.1 Gene Therapy for Treatment of Spinal Muscular Atrophy
7.1.2 MRI for SMA Detection
7.1.3 Strategic Collaboration to Develop Novel Small Molecule RNA Splicing Modifiers
7.2 Growth Drivers
7.2.1 Rising Incidences of Spinal Muscular Atrophy (SMA)
7.2.2 Government Impetus
7.2.3 Growing Consumer Awareness
7.2.5 Increasing Funding for R&D
7.3 Challenges
7.3.1 High Cost of Therapy
7.3.2 Low Market Penetration of Drug Therapy
8. Competitive Landscape
9. Company Profiles
9.1 Biogen Inc.
9.2 Cytokinetics, Inc.
9.3 AveXis, Inc.(Novartis AG)
9.4 F. Hoffmann-La Roche AG
9.5 Ionis Pharmaceuticals, Inc.